this post was submitted on 18 Jan 2024
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The world's 1st CRISPR therapy has been approved. Here's everything you need to know (www.livescience.com)
submitted 10 months ago by fukhueson@lemmy.world to c/science@lemmy.world
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[–] solrize@lemmy.world 18 points 10 months ago

Exa-cel, also known by its brand name Casgevy, received its first regulatory approval on Nov. 16, 2023 from the U.K. Medicines and Healthcare products Regulatory Agency (MHRA) to treat two debilitating blood disorders: sickle-cell disease and transfusion-dependent beta-thalassemia. The U.S. Food and Drug Administration (FDA) later approved the therapy as a treatment for both disorders.